Tuesday, September 5
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15:00 to 17:00
Registration
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17:00 to 18:00
Keynote: Modifying Genomic DNA and RNA
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18:00 to 19:30
Opening Reception
Wednesday, September 6
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8:30 to 10:30
Therapeutic Targeting of RNA
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10:30 to 11:00
Coffee Break - Green Room
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11:00 to 11:30
Epigenetic Mechanisms in Congenital Myotonic Dystrophy
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11:30 to 12:30
DM Session 1: Microsatellite Instability and Epigenetics
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12:30 to 13:00
Flash Poster Session
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13:00 to 14:30
Poster Viewing
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14:30 to 17:00
DM Session 2: Disease Mechanisms DM1, DM2 and CDM
Thursday, September 7
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8:30 to 9:00
Pathogenic Mechanisms of C9orf72 Repeat Expansion
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9:30 to 10:00
DM Session 3: Cancer and Aging in DM
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10:00 to 10:30
Coffee Break - Green Room
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10:30 to 12:00
DM Session 4: Clinical, Ethical and Social Issues, and Disease Burden
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12:00 to 12:30
Flash Poster Session
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12:30 to 14:00
Poster Viewing
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14:00 to 16:30
DM Session 5: Specific Disease Features: CNS, Cardiac and GI
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16:30 to 17:00
Organization and Outreach Update
Friday, September 8
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8:30 to 9:30
CNS and Sleep
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9:30 to 10:30
DM Session 6: Cell Models for DM
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10:30 to 11:00
Coffee Break - Green Room
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11:00 to 12:00
DM Session 7: Animal Models and Tissue-specific Mechanisms
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12:00 to 12:30
Flash Poster Session
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12:30 to 13:30
Poster Viewing
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13:30 to 16:30
Neuromuscular Clinical Research Experience
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16:30 to 17:30
DM Session 8: RNA Clinical Research Methods: Biomarkers, Outcome Measures, Registries, Trial Design and Therapeutics
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19:30 to 21:30
Closing Dinner
Saturday, September 9
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7:00 to 9:00
Drug Development Roundtable
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8:00 to 9:00
Breakfast and MDF Research Update
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9:45 to 10:00
Coffee Break
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10:00 to 12:00
Bringing the Patient Voice to CNS-Targeting Drug Development in Myotonic Dystrophy
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12:00 to 13:00
Bringing the Patient Voice to CNS - Facilitated Lunch Discussion and Report Out
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13:00 to 13:45
Grant Writing Training
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15:30 to 17:00
Expanding the Pipeline: Industry Updates on Drug Development